New Hope: Using Gene Therapy to Treat Rare Neurological Diseases
https://doi.org/10.52667/2712-9179-2023-3-1-3-6
Abstract
Gene therapy is a promising treatment approach for rare/orphan neurological diseases that have limited treatment options and no cure. This article provides a brief overview of different types of rare hereditary neurological diseases and discusses existing gene therapy drugs approved for their treatment. Despite challenges associated with the development and implementation of gene therapy, including cost, delivery, and long-term safety and efficacy, the potential benefits of gene therapy make it a compelling area of research for the treatment of rare hereditary neurological diseases.
Supporting agencies: This paper has been supported by the Kazan Federal University Strategic Academic Leadership Program (PRIORITY-2030).
About the Author
A. A Rizvanov
Kazan Federal University
Russian Federation
Russian Federation
Albert A. Rizvanov
Kazan
Tel.: +7 (843) 293-43-07
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Review
For citations:
Rizvanov A.A. New Hope: Using Gene Therapy to Treat Rare Neurological Diseases. Personalized Psychiatry and Neurology. 2023;3(1):3-6. https://doi.org/10.52667/2712-9179-2023-3-1-3-6
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